CPC C12N 15/113 (2013.01) [A61K 31/7088 (2013.01); A61K 31/713 (2013.01); A61K 47/549 (2017.08); C07H 21/04 (2013.01); C12N 15/111 (2013.01); C12N 2310/11 (2013.01); C12N 2310/113 (2013.01); C12N 2310/17 (2013.01); C12N 2310/31 (2013.01); C12N 2310/315 (2013.01); C12N 2310/321 (2013.01); C12N 2310/322 (2013.01); C12N 2310/3231 (2013.01); C12N 2310/3341 (2013.01); C12N 2310/341 (2013.01); C12N 2310/346 (2013.01); C12N 2310/351 (2013.01); C12N 2310/353 (2013.01); C12N 2310/3511 (2013.01); C12N 2310/3513 (2013.01); C12N 2310/3515 (2013.01); C12N 2310/3525 (2013.01); C12N 2320/32 (2013.01)] | 33 Claims |
1. A compound or a salt thereof comprising a modified oligonucleotide and a conjugate group, wherein the modified oligonucleotide consists of 12 to 30 linked nucleosides and comprises a nucleobase sequence comprising a portion of at least 8 contiguous nucleobases complementary to an equal length portion of nucleobases 3901 to 3920 of SEQ ID NO: 1, wherein the nucleobase sequence of the modified oligonucleotide is at least 80% complementary to SEQ ID NO: 1; and wherein the conjugate group comprises:
wherein each n is, independently, an integer from 1 to 20.
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