| CPC C12Q 1/6816 (2013.01) [C07H 21/02 (2013.01); C12N 9/22 (2013.01); C12N 15/11 (2013.01); C12N 15/85 (2013.01); C12N 2310/20 (2017.05); C12N 2310/3519 (2013.01); C12N 2830/003 (2013.01); C12Q 2600/156 (2013.01)] | 26 Claims |
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1. A composition, comprising:
i) a cell comprising a deoxyribonucleic acid (DNA) repeat expansion sequence;
ii) a nuclease-dead Cas9 (dCas) fusion protein bound to a labeled peptide or labeled protein; and
iii) a single guide ribonucleic acid (sgRNA) comprising a stem loop, said stem loop having at least one A-U pair replaced with a G-C pair, wherein said sgRNA is complementary to at least a portion of said deoxyribonucleic acid (DNA) repeat expansion sequence.
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