CPC C12N 15/902 (2013.01) [C12N 9/22 (2013.01); C12N 15/113 (2013.01); C12N 15/8213 (2013.01); C12N 2310/20 (2017.05); C12N 2310/3519 (2013.01)] | 7 Claims |
1. A method for genetically modifying a cell, comprising:
introducing into the cell a genome editing system for site-directed modification of a target sequence, wherein the Cas9 nuclease variant is targeted to the target sequence in the genome of the cell by the guide RNA, and results in substitution, deletion and/or addition of one or more nucleotides in the target sequence,
wherein the genome editing system comprises at least one selected from the following (i) to (iii):
(i) a Cas9 nuclease variant, and an expression construct comprising a nucleotide sequence encoding a tRNA-guide RNA fusion;
(ii) an expression construct comprising a nucleotide sequence encoding a Cas9 nuclease variant, and an expression construct comprising a nucleotide sequence encoding a tRNA-guide RNA fusion; and
(iii) an expression construct comprising a nucleotide sequence encoding a Cas9 nuclease variant and a nucleotide sequence encoding a tRNA-guide RNA fusion;
wherein the Cas9 nuclease variant has higher specificity as compared with the wild-type Cas9 nuclease, wherein the Cas9 nuclease variant comprises the amino acid sequence as set forth in SEQ ID NO: 4, SEQ ID NO: 5 or SEQ ID NO: 6; wherein the 5′ end of the guide RNA is linked to the 3′ end of the tRNA, and the guide RNA is 20 nt in length; and wherein the fusion of guide RNA and the tRNA is cleaved at the 5′ end of the guide RNA after being transcribed in the cell, thereby forming a guide RNA that does not carry an extra nucleotide at the 5′ end.
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