| CPC C12N 15/87 (2013.01) [A61K 35/28 (2013.01); C08K 5/5399 (2013.01); C12N 5/0647 (2013.01); C12N 5/0657 (2013.01); C12N 5/0696 (2013.01); C12N 9/16 (2013.01); C12N 9/22 (2013.01); C12N 15/907 (2013.01); C12P 21/00 (2013.01); C12Y 301/21 (2013.01); H10F 19/80 (2025.01); A61K 2035/124 (2013.01); C08G 77/08 (2013.01); C12N 2500/25 (2013.01); C12N 2500/44 (2013.01); C12N 2501/115 (2013.01); C12N 2501/155 (2013.01); C12N 2501/165 (2013.01); C12N 2501/2303 (2013.01); C12N 2501/26 (2013.01); C12N 2501/91 (2013.01); C12N 2501/998 (2013.01); C12N 2506/09 (2013.01); C12N 2800/80 (2013.01); Y02E 10/50 (2013.01)] | 20 Claims |
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1. A method for generating gene-edited cells, the method comprising:
(a) providing a plurality of cells comprising a target DNA sequence, wherein the plurality of cells is derived from a human subject;
(b) culturing the plurality of cells under conditions that allow the plurality of cells to proliferate; and
(c) contacting the plurality of cells in vitro or ex vivo with a plurality of synthetic RNA molecules,
wherein the plurality of synthetic RNA molecules comprises a nucleotide sequence that encodes a transcription activator-like effector nuclease,
wherein the plurality of synthetic RNA molecules is added to a medium surrounding the plurality of cells, and
wherein the contacting results in the plurality of cells internalizing the plurality of synthetic RNA molecules and expressing the transcription activator-like effector nuclease to result in a single-strand break or a double-strand break in the target DNA sequence, thereby generating the gene-edited cells.
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