| CPC A61K 47/6909 (2017.08) [A61K 31/575 (2013.01); A61K 31/661 (2013.01); C12N 15/113 (2013.01)] | 10 Claims |

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1. A method for delivery of mRNA or vector DNA for in vivo production of protein or peptide in the liver, the method comprising administering to a mammal a lipid nanoparticle having 49 to 85 mol % of a sterol or a derivative thereof, a phospholipid or a phospholipid-sterol conjugate at 0 to 7 mol % that is in a neutral zwitterionic form at physiological pH, an ionizable lipid and a hydrophilic polymer-lipid conjugate present at 0.5 to 1.8 mol %, wherein the mRNA or vector DNA is encapsulated within the lipid nanoparticle and wherein the administering of the lipid nanoparticle results in liver-specific expression of the protein or peptide encoded by the mRNA or vector DNA, wherein the lipid nanoparticle has increased expression of the protein or peptide encoded by the mRNA or vector DNA in the liver over the spleen by at least 20-fold.
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