US 11,946,065 B2
Transgene cassettes, AAV vectors, and AAV viral vectors for expression of human codon-optimized CSTB
Berge A. Minassian, Dallas, TX (US); and Emrah Gumusgoz, Dallas, TX (US)
Assigned to THE BOARD OF REGENTS OF THE UNIVERSITY OF TEXAS SYSTEM, Austin, TX (US)
Filed by THE BOARD OF REGENTS OF THE UNIVERSITY OF TEXAS SYSTEM, Austin, TX (US)
Filed on Jul. 28, 2021, as Appl. No. 17/387,035.
Claims priority of provisional application 63/058,038, filed on Jul. 29, 2020.
Prior Publication US 2022/0049270 A1, Feb. 17, 2022
Int. Cl. C12N 15/864 (2006.01); C12N 7/00 (2006.01); C12N 15/11 (2006.01); C12N 15/113 (2010.01); C12N 15/15 (2006.01); C12N 15/86 (2006.01)
CPC C12N 15/86 (2013.01) [C12N 7/00 (2013.01); C12N 2750/14143 (2013.01); C12N 2750/14151 (2013.01)] 13 Claims
 
1. An expression cassette comprising:
(a) SEQ ID NO:9;
(b) SEQ ID NO:3, and SEQ ID NO:9; or
(c) SEQ ID NO:2, SEQ ID NO:3, SEQ ID NO:9, SEQ ID NO:10, SEQ ID NO:11, SEQ ID NO:13, and SEQ ID NO:14.