Gene editing components, systems, and methods of use
Giedrius Gasiunas, Vilnius (LT); Alim Ladha, Cambridge, MA (US); Vladimir Presnyak, Cambridge, MA (US); Muthusamy Jayaraman, Cambridge, MA (US); and Elisabeth Narayanan, Cambridge, MA (US)
Assigned to ReNAgade Therapeutics Management, Inc., Cambridge, MA (US)
Filed by ReNAgade Therapeutics Management Inc., Cambridge, MA (US)
Filed on Oct. 5, 2023, as Appl. No. 18/481,393.
Application 18/481,393 is a continuation of application No. PCT/US2023/070339, filed on Jul. 17, 2023.
Application PCT/US2023/070339 is a continuation in part of application No. 18/297,346, filed on Apr. 7, 2023.
Claims priority of provisional application 63/495,198, filed on Apr. 10, 2023.
Claims priority of provisional application 63/368,728, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,737, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,736, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,730, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,731, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,744, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,724, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,734, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,735, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,722, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,726, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,742, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,738, filed on Jul. 18, 2022.
Claims priority of provisional application 63/368,741, filed on Jul. 18, 2022.
1. An isolated or recombinant polynucleotide comprising:
a nucleic acid sequence that encodes a polypeptide at least 95% identical to SEQ ID NO: 585, wherein the polypeptide comprises arginine (R) at position 169.