| CPC C07K 16/2896 (2013.01) [A61K 40/17 (2025.01); A61K 40/24 (2025.01); A61K 40/31 (2025.01); A61K 40/4205 (2025.01); A61K 40/4224 (2025.01); A61P 35/00 (2018.01); C07K 14/70578 (2013.01); C07K 16/2863 (2013.01); C12N 5/0645 (2013.01); C12N 9/1205 (2013.01); C12N 15/87 (2013.01); A61K 2239/38 (2023.05); A61K 2239/48 (2023.05); C07K 2317/52 (2013.01); C07K 2317/622 (2013.01); C07K 2319/03 (2013.01)] | 17 Claims |
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1. A pharmaceutical composition comprising:
(a) a population of mRNA-electroporated cells lacking a viral component or a plasmid component, wherein the mRNA comprises a sequence encoding a chimeric fusion protein (CFP) or a sequence encoding an antigenic peptide, wherein:
(i) at least 50% of the cells in the population of mRNA-electroporated cells are CD 14+;
(ii) less than 10% of the cells in the population of mRNA-electroporated cells are dendritic cells; and
(iii)
(A) at least 50% of the cells in the population of mRNA-electroporated cells are CCR2+ (CD192+), and CCR5+ (CD195+) and two or more of: CD63+, CD56 CD120a+ (TNFR1+) or CD120b+ (TNFR2+);
(B) less than 50% of the cells in the population of mRNA-electroporated cells express CD64 CD68, CD80, CD86, CD163, CD206, CD200R, CD31, CD71, CLEC9A, CD1C for AXL/SIGLEC6;
(C) when the mRNA comprises a sequence encoding a CFP and the population of mRNA-electroporated cells are in the presence of cells expressing a cell-surface antigen to which the CFP specifically binds, the population of mRNA-electroporated cells one or more cytokines selected from the group consisting of IL-1beta, TNFalpha, IFN-alpha, MIP-1alpha, IL-8, eotaxin, PIGF-1, CCL3, IL6 and IL10; and
(D) when the mRNA comprises a sequence encoding a CFP and the population of mRNA-electroporated cells are in the presence of GMCSF, IL-4 IL-10, TGFbeta TCM and/or MCSF, the expression of MHCI or MHCII is upregulated in the population of mRNA-electroporated cells to a greater extent compared to a corresponding population of cells that have not been electroporated with the mRNA; and
(b) a pharmaceutically acceptable excipient; and
wherein when the mRNA comprises a sequence encoding a CFP, the population of mRNA-electroporated cells in the pharmaceutical composition do not exhibit tonic signaling through the CFP ex vivo.
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