CPC C12N 15/113 (2013.01) [A61K 9/0048 (2013.01); A61P 27/02 (2018.01); C12N 15/86 (2013.01); C12N 2310/11 (2013.01); C12N 2310/20 (2017.05); C12N 2310/314 (2013.01); C12N 2310/315 (2013.01); C12N 2310/321 (2013.01); C12N 2750/14143 (2013.01)] | 21 Claims |
1. A pharmaceutical composition comprising:
(a) a pharmaceutically acceptable excipient; and
(b) a therapeutic agent, wherein the therapeutic agent comprises an antisense oligomer that comprises the sequence set forth in any one of SEQ ID NO: 36, 92-96, or 166-168, and wherein the antisense oligomer comprises a 2′-O-methoxyethyl moiety.
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